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Amicus Therapeutics' CEO John F. Crowley to Advocate for Rare and Orphan Disease Community in Washington, D.C. This Week (0 Comments)

Date: 
09/12/2013

Amicus Therapeutics (FOLD) today announced that John F. Crowley, Chairman and Chief Executive Officer, will advocate for the rare and orphan disease community at several upcoming events in Washington, D.C tomorrow on September 12, 2013

CRANBURY, N.J., Sept. 11, 2013 (GLOBE NEWSWIRE) -- Amicus Therapeutics (FOLD) today announced that John F. Crowley, Chairman and Chief Executive Officer, will advocate for the rare and orphan disease community at several upcoming events in Washington, D.C tomorrow on September 12, 2013:

Rare Disease Congressional Caucus Briefing

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Rare LCHAD Disorder Means Two-Year-Old Must Eat Every Hour (1 Comment)

Date: 
11/09/2015

November 9, 2015 By Ilana Jacqueline Leave a Comment

To all the new parents struggling to feed their newborn every two to three hours, imagine having to do it every hour—for years. Such is reality for the Torti family in Tennessee, whose son, Owen, now 23 months, was diagnosed with the rare metabolic disorder…

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Prader-Willi Patients Have New Opportunity to Enter Clinical Trial (0 Comments)

Date: 
11/10/2015

November 10, 2015 By Ilana Jacqueline Leave a Comment

Late for lunch, not enough for dinner–we may think we’re familiar with the sensation of hunger, but for patients with Prader-Willi Syndrome, hunger is a whole different animal. The complex genetic disease shows it’s first signs with weak muscle tone, delayed development and poor growth.…

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Sydney Markets Fruit Auction Raises $75,000 for Duchenne Muscular Dystrophy (0 Comments)

Date: 
11/10/2015

November 10, 2015 By Ilana Jacqueline Leave a Comment

Sydney Market wholesalers have raised more than $75,000 for charity at a special auction including summer fruits. The money raised goes to Save Our Sons, the charity supporting sufferers of Duchenne Muscular Dystrophy (DMD). The muscle-wasting condition affects one in 3,500 boys, with the onset appearing…

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